Videos
Information
- Regenxbio Fact Sheet
- JCR Fact Sheet
- Denali Fact Sheet
- Homology Fact Sheet
- Avrobio Fact Sheet
- UCSF In Utero ERT
- Takeda Hunter Syndrome Info
Resources:
- National MPS Society: A Guide to Understanding MPS II
- Urbatsch Law Firm – Family/Financial Planning
- Siblings with a Mission
- Angel Aid Cares